Real-world treatment with Zolgensma improves motor function in SMA children who carry at least four copies of the so-called ...

Columnist Ari Anderson shares some exciting news about a new home and his family's efforts to create adaptive living spaces.

A high-dose Spinraza treatment regimen was shown in a trial to safely improve motor function in untreated babies with spinal ...

Living with SMA can take a toll on columnist Alyssa Silva's mental health, but she finds refuge and peace in trips to the ...

Going to the emergency room is uncommon for columnist Helen Baldwin, but it's always emotional, a reminder of her late son, ...

Children with spinal muscular atrophy (SMA) exhibit widespread metabolic disruption — changes that affect the body’s ...

As an SMA patient, columnist Sherry Toh is reminded how her usual medical team makes all the difference when she's struggling ...

An SMA Europe awareness initiative - the documentary “One Community. Shared Dreams.” - highlights the need for researchers to ...

We can live in solitude or engage with the world, columnist Kevin Schaefer writes. That's your mission, should you choose to ...

Patients with spinal muscular atrophy (SMA) in China and their caregivers have low levels of health information literacy, or the ability to access, understand, evaluate, and use information to make ...